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Leukodystrophy, Metachromatic

Showing 1 - 25 of 55
STUDY
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Lysosomal Storage Disease, Metachromatic Leukodystrophy Trial in Milan (OTL-200 Gene Therapy)

Active, not recruiting
  • Lysosomal Storage Disease
  • Metachromatic Leukodystrophy
  • OTL-200 Gene Therapy
  • Milan, Italy
    Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR
Nov 4, 2022

Lysosomal Storage Diseases, Metachromatic Leukodystrophy Trial in Milan (OTL-200)

Recruiting
  • Lysosomal Storage Diseases
  • Metachromatic Leukodystrophy
  • OTL-200
  • Milan, Italy
    Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR
Nov 16, 2022

Macrophages Activation Pattern in X-linked Adrenoleukodystrophy,

Recruiting
  • Adrenoleukodystrophy
  • +3 more
  • Blood sample collection
  • Le Kremlin-Bicêtre, France
  • +1 more
Oct 10, 2022

Learn About Metachromatic Leukodystrophy (MLD) in Spain

Not yet recruiting
  • Metachromatic Leukodystrophy (MLD)
  • No Intervention
  • Santiago de Compostela, A Coruna, Spain
  • +9 more
Mar 9, 2023

Metachromatic Leukodystrophy, Adrenoleukodystrophy Trial in Shenzhen (transduced CD34+ hematopoietic stem cell)

Recruiting
  • Metachromatic Leukodystrophy
  • Adrenoleukodystrophy
  • transduced CD34+ hematopoietic stem cell
  • Shenzhen, Guangdong, China
    Shenzhen Second People's Hospital, The First Affiliated Hospital
May 25, 2022

Metachromatic Leukodystrophy Trial in Durham (Enriched Hematopoetic Stem Cell Infusion)

No longer available
  • Metachromatic Leukodystrophy
  • Enriched Hematopoetic Stem Cell Infusion
  • Durham, North Carolina
    Duke University
Jul 15, 2022

Metachromatic Leukodystrophy Trial in Le Kremlin-Bicêtre (intracerebral administration of AAVrh.10cuARSA)

Active, not recruiting
  • Metachromatic Leukodystrophy
  • intracerebral administration of AAVrh.10cuARSA
  • Le Kremlin-Bicêtre, France
    Bicêtre Hospital - Paris Sud
Jan 10, 2022

Adrenoleukodystrophy, Batten Disease, Mucopolysaccharidosis II Trial in Durham (DUOC-01)

Recruiting
  • Adrenoleukodystrophy
  • +11 more
  • DUOC-01
  • Durham, North Carolina
    Duke University Medical Center
Oct 24, 2022

Metachromatic Leukodystrophy Study (HOME Study)

Recruiting
  • Metachromatic Leukodystrophy
    • Danbury, Connecticut
      National Organization for Rare Disorders
    Oct 28, 2021

    Lysosomal Storage Disease, Metachromatic Leukodystrophy Trial in Milan (OTL-200)

    Active, not recruiting
    • Lysosomal Storage Disease
    • Metachromatic Leukodystrophy
    • OTL-200
    • Milan, Italy
      Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR
    Sep 29, 2021

    Metachromatic Leukodystrophy (MLD) Trial in Worldwide (SHP611)

    Active, not recruiting
    • Metachromatic Leukodystrophy (MLD)
    • Torrance, California
    • +29 more
    Dec 13, 2022

    Mucopolysaccharidosis I, Mucopolysaccharidosis VI, Adrenoleukodystrophy Trial in Denver, Valhalla, Salt Lake City (Human

    Completed
    • Mucopolysaccharidosis I
    • +15 more
    • Human Placental Derived Stem Cell
    • Denver, Colorado
    • +2 more
    Oct 24, 2022

    Metachromatic Leukodystrophy (MLD) Trial in Hvidovre (rhASA - Dose Level 1, rhASA - Dose Level 2, rhASA - Dose Level 3)

    Completed
    Has Results
    • Metachromatic Leukodystrophy (MLD)
    • rhASA - Dose Level 1
    • +2 more
    • Hvidovre, Denmark
      Rigshospitalet
    Jun 23, 2021

    Mucopolysaccharidosis Disorders, Hurler Syndrome, Hunter Syndrome Trial in Minneapolis (Stem Cell Transplantation, IMD

    Recruiting
    • Mucopolysaccharidosis Disorders
    • +28 more
    • Stem Cell Transplantation
    • +7 more
    • Minneapolis, Minnesota
      Masonic Cancer Center, University of Minnesota
    Nov 1, 2022

    Biomarker for Metachromatic Leukodystrophy (BioMeta) Disease

    Active, not recruiting
    • Peripheral Neuropathy
    • Muscle Weakness
      • Cairo, Egypt
      • +4 more
      May 12, 2021

      Leukodystrophy, White Matter Disease, Leukoencephalopathies Trial in United States

      Recruiting
      • Leukodystrophy
      • +21 more
        • Palo Alto, California
        • +8 more
        Dec 21, 2021

        Children With Metachromatic Leukodystrophy

        Terminated
        • Lipid Metabolism Disorders
        • +13 more
          • Torrance, California
          • +13 more
          Mar 16, 2021

          ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn

          Enrolling by invitation
          • Acid Sphingomyelinase Deficiency
          • +13 more
          • Confirmatory Testing
          • Bronx, New York
          • +9 more
          May 9, 2022

          Metachromatic Leukodystrophy Trial in Durham (Enriched Hematopoetic Stem Cell Infusion)

          No longer available
          • Metachromatic Leukodystrophy
          • Enriched Hematopoetic Stem Cell Infusion
          • Durham, North Carolina
            Duke University
          Oct 6, 2020

          Hurler Syndrome, Inherited Metabolic Disorder, Lysosomal Storage Disorder Trial in Los Angeles, Palo Alto (rivogenlecleucel,

          No longer available
          • Hurler Syndrome
          • +4 more
          • Los Angeles, California
          • +1 more
          Oct 1, 2020

          Baby Detect : Genomic Newborn Screening

          Recruiting
          • Congenital Adrenal Hyperplasia
          • +126 more
            • Liege, Wallonia, Belgium
              CRMN, Hôpital La Citadelle
            Jan 24, 2023

            Metachromatic Leukodystrophy (MLD) Trial in Shenzhen (Lentivirus-mediated delivery of ARSA to the CNS.)

            Unknown status
            • Metachromatic Leukodystrophy (MLD)
            • Lentivirus-mediated delivery of ARSA to the CNS.
            • Shenzhen, Guangdong, China
              Lung-Ji Chang
            Sep 18, 2019

            Adrenoleukodystrophy, Metachromatic Leukodystrophy, Globoid Cell Leukodystrophy Trial in Minneapolis (drug, procedure,

            Completed
            Has Results
            • Adrenoleukodystrophy
            • +8 more
            • Minneapolis, Minnesota
              Masonic Cancer Center, University of Minnesota
            Jul 10, 2019

            Leukodystrophy: An Observational Study at Sohag University

            Not yet recruiting
            • Children With Leukodystrophy
            • MRI
            • (no location specified)
            Mar 2, 2021

            Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

            Recruiting
            • Primary Immunodeficiency (PID)
            • +4 more
            • data collection
            • Pittsburgh, Pennsylvania
              UPMC Children's Hospital of Pittsburgh
            Feb 9, 2022